Prevention of systemic clinical disease in mps vii mice following aav-mediated neonatal gene transfer

Prevention of systemic clinical disease in mps vii mice following aav-mediated neonatal gene transfer


Play all audios:


Gene therapy trials give mixed messages. Access through your institution Buy or subscribe This is a preview of subscription content, access via your institution ACCESS OPTIONS Access through


your institution Subscribe to this journal Receive 51 print issues and online access $199.00 per year only $3.90 per issue Learn more Buy this article * Purchase on SpringerLink * Instant


access to full article PDF Buy now Prices may be subject to local taxes which are calculated during checkout ADDITIONAL ACCESS OPTIONS: * Log in * Learn about institutional subscriptions *


Read our FAQs * Contact customer support REFERENCES * Daly, T.M. et al. Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer. _Gene Therapy_


8, 1291 - 1298 (2001). Article  CAS  Google Scholar  * Song, S. et al. Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant


adeno-associated virus (rAAV) vectors. _Gene Therapy_ 8, 1299 - 1306 (2001). Article  CAS  Google Scholar  * Donsante, A. et al. Observed incidence of tumourigenesis in long-term rodent


studies of rAAV vectors. _Gene Therapy_ 8, 1343 - 1346 (2001). Article  CAS  Google Scholar  Download references RIGHTS AND PERMISSIONS Reprints and permissions ABOUT THIS ARTICLE CITE THIS


ARTICLE Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer. _Nature_ (2001). https://doi.org/10.1038/news010906-13 Download citation *


Published: 05 September 2001 * DOI: https://doi.org/10.1038/news010906-13 SHARE THIS ARTICLE Anyone you share the following link with will be able to read this content: Get shareable link


Sorry, a shareable link is not currently available for this article. Copy to clipboard Provided by the Springer Nature SharedIt content-sharing initiative